An Antisense Oligonucleotide for Hereditary Angioedema

N Engl J Med. 2022 Mar 17;386(11):1083-1085. doi: 10.1056/NEJMe2201729.
No abstract available

Publication types

  • Editorial
  • Comment

MeSH terms

  • Angioedemas, Hereditary* / genetics
  • Complement C1 Inhibitor Protein
  • Humans
  • Oligonucleotides / therapeutic use
  • Oligonucleotides, Antisense / therapeutic use

Substances

  • Complement C1 Inhibitor Protein
  • Oligonucleotides
  • Oligonucleotides, Antisense