Abstract
Lysosomal storage disorders (LSDs) are rare, monogenic diseases characterized by aberrant lysosomes with storage material [...].
Publication types
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Editorial
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Introductory Journal Article
MeSH terms
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Animals
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Autophagy
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Clinical Trials as Topic
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Disease Models, Animal
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Enzyme Replacement Therapy
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Humans
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Lysosomal Storage Diseases / therapy*
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Organelles / metabolism
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Pathology, Molecular*