1 Department of Pediatrics, National Taiwan University Hospital and National Taiwan University College of Medicine, Taipei, Taiwan. Electronic address: hwuwlntu@ntu.edu.tw.
2 Division of Neurological Gene Therapy, Center for Open Innovation, Jichi Medical University, Tochigi, Japan.
3 Department of Pediatrics, National Taiwan University Hospital and National Taiwan University College of Medicine, Taipei, Taiwan.
4 Department of Pediatrics, College of Medicine, Powell Gene Therapy Center, University of Florida, Gainesville, USA.