Gene therapy reforms photoreceptor structure and restores vision in NPHP5-associated Leber congenital amaurosis
Mol Ther
.
2021 Dec 1;29(12):3528.
doi: 10.1016/j.ymthe.2021.10.021.
Epub 2021 Oct 29.
Authors
Gustavo D Aguirre
,
Artur V Cideciyan
,
Valérie L Dufour
,
Ana Ripolles-García
,
Raghavi Sudharsan
,
Malgorzata Swider
,
Roman Nikonov
,
Simone Iwabe
,
Sanford L Boye
,
William W Hauswirth
,
Samuel G Jacobson
,
William A Beltran
PMID:
34715016
PMCID:
PMC8636161
DOI:
10.1016/j.ymthe.2021.10.021
No abstract available
Publication types
Published Erratum
Grants and funding
P30 EY001583/EY/NEI NIH HHS/United States