Rational design of cell active C2-modified DGJ analogues for the inhibition of human α-galactosidase A (GALA)

Org Biomol Chem. 2021 Sep 29;19(37):8057-8062. doi: 10.1039/d1ob01526e.

Abstract

We report the rational design and synthesis of C2-modified DGJ analogues to improve the selective inhibition of human GALA over other glycosidases. We prepare these analogues using a concise route from non-carbohydrate materials and demonstrate the most selective inhibitor 7c (∼100-fold) can act in Fabry patient cells to drive reductions in levels of the disease-relevant glycolipid Gb3.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • alpha-Galactosidase*

Substances

  • alpha-Galactosidase