No abstract available
Keywords:
nusinersen; onasemnogene abeparvovec; risdiplam.
Publication types
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Research Support, Non-U.S. Gov't
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Review
MeSH terms
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Adolescent
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Adult
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Azo Compounds / therapeutic use
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Biological Products / therapeutic use
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Child
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Child, Preschool
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Humans
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Infant
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Infant, Newborn
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Neuromuscular Agents / therapeutic use
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Oligonucleotides / therapeutic use
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Pyrimidines / therapeutic use
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Recombinant Fusion Proteins / therapeutic use
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Spinal Muscular Atrophies of Childhood / diagnosis
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Spinal Muscular Atrophies of Childhood / etiology
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Spinal Muscular Atrophies of Childhood / therapy*
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Young Adult
Substances
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Azo Compounds
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Biological Products
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Neuromuscular Agents
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Oligonucleotides
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Pyrimidines
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Recombinant Fusion Proteins
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Zolgensma
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nusinersen
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Risdiplam