Preparation of Lipid-Conjugated siRNA Oligonucleotides for Enhanced Gene Inhibition in Mammalian Cells

Methods Mol Biol. 2021:2282:119-136. doi: 10.1007/978-1-0716-1298-9_8.

Abstract

Nucleic acid conjugates are promising drugs for treating gene-related diseases. Conjugating specific units like lipids, cell-penetrating peptides, polymers, antibodies, and aptamers either at the 3'- or 5'-termini of a siRNA duplex molecule has resulted in a plethora of siRNA bioconjugates with improved stabilities in bloodstream and better pharmacokinetic values than unmodified siRNAs. In this sense, lipid-siRNA conjugates have attracted a remarkable interest for their potential value in facilitating cellular uptake. In this chapter, we describe a series of protocols involving the synthesis of siRNA oligonucleotides carrying either neutral or cationic lipids at the 3'- and 5'-termini. The resulting lipid-siRNA conjugates are aimed to be used as exogenous effectors for inhibiting gene expression by RNA interference. A protocol for the formulation of lipid siRNA using sonication in the presence of serum is described yielding interesting transfection properties for cell culture without the use of transfecting agents.

Keywords: Lipids; Phosphoramidite chemistry; RNA interference; Serum; Ultrasounds; siRNA conjugates; siRNA delivery.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Breast Neoplasms / genetics
  • Breast Neoplasms / metabolism
  • Female
  • Gene Expression Regulation, Neoplastic
  • Gene Transfer Techniques*
  • HeLa Cells
  • Humans
  • Lipids / chemistry*
  • Mice
  • Oligonucleotides / chemical synthesis*
  • Oligonucleotides / genetics
  • Oligonucleotides / metabolism
  • Organophosphorus Compounds / chemistry*
  • RNA Interference*
  • RNA, Small Interfering / chemical synthesis*
  • RNA, Small Interfering / genetics
  • RNA, Small Interfering / metabolism
  • Research Design
  • Sonication
  • Tumor Necrosis Factor-alpha / genetics
  • Tumor Necrosis Factor-alpha / metabolism
  • Uterine Cervical Neoplasms / genetics
  • Uterine Cervical Neoplasms / metabolism
  • Workflow

Substances

  • Lipids
  • Oligonucleotides
  • Organophosphorus Compounds
  • RNA, Small Interfering
  • TNF protein, human
  • Tnf protein, mouse
  • Tumor Necrosis Factor-alpha
  • phosphoramidite