A pause in gene therapy: Reflecting on the unique challenges of sickle cell disease

Mol Ther. 2021 Apr 7;29(4):1355-1356. doi: 10.1016/j.ymthe.2021.03.010. Epub 2021 Mar 19.

Authors

Alexis Leonard¹, John F Tisdale²

Affiliations

¹ Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD, USA.
² Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD, USA. Electronic address: johntis@nhlbi.nih.gov.

No abstract available

Publication types

Editorial

MeSH terms

Anemia, Sickle Cell / genetics
Anemia, Sickle Cell / therapy*
Genetic Therapy / trends*
Humans