Platelet-derived growth factor C signaling is a potential therapeutic target for radiation proctopathy

Sci Transl Med. 2021 Feb 24;13(582):eabc2344. doi: 10.1126/scitranslmed.abc2344.

Abstract

Radiation proctopathy (RP) is characterized by inflammation of colorectal tissue and is a common complication of radiation therapy for pelvic malignancies with high incidence but lacking effective treatment. Here, we found that platelet-derived growth factor C (PDGF-C) and fibrosis markers were up-regulated in tissue samples from patients with RP and in rectal tissues after irradiation in a mouse model of RP. Genetic deletion of Pdgf-c in mice ameliorated RP-induced injuries. Genome-wide gene expression profiling and in vitro assays revealed that the promotive effect of PDGF-C in RP development was mediated by activation of PDGF receptors (PDGFRs) and C-X-C motif chemokine receptor 4, a proinflammatory chemokine regulated by transcription factor ETS variant transcription factor 1. Treatment with crenolanib, a selective inhibitor of PDGFRs, prevented or reduced RP in mice after irradiation. These results reveal that inhibition of PDGF-C signaling may have therapeutic value for the treatment of RP.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Humans
  • Lymphokines*
  • Mice
  • Platelet-Derived Growth Factor*
  • Radiation Injuries / therapy*
  • Receptors, Platelet-Derived Growth Factor / metabolism
  • Rectum / pathology*
  • Rectum / radiation effects
  • Signal Transduction

Substances

  • Lymphokines
  • Platelet-Derived Growth Factor
  • platelet-derived growth factor C
  • Receptors, Platelet-Derived Growth Factor