Small molecule drugs in cystic fibrosis
Arch Dis Child Educ Pract Ed
.
2022 Oct;107(5):379-382.
doi: 10.1136/archdischild-2020-319009.
Epub 2020 Nov 19.
Authors
Christopher Hine
1
,
Prasad Nagakumar
2
3
,
Maya Desai
2
Affiliations
1
Paediatric Respiratory Medicine Department, Birmingham Children's Hospital, Birmingham, West Midlands, UK christopher.hine@nhs.net.
2
Paediatric Respiratory Medicine Department, Birmingham Children's Hospital, Birmingham, West Midlands, UK.
3
Birmingham Acute Care Research Group, Institute of Inflammation and Ageing, University of Birmingham, Birmingham, UK.
PMID:
33214241
DOI:
10.1136/archdischild-2020-319009
No abstract available
Keywords:
cystic fibrosis; genetics; pharmacology.
MeSH terms
Cystic Fibrosis* / drug therapy
Humans
Mutation