Getting Back to Normal: Correcting SCN by Universal or Precision Strikes

Mol Ther. 2020 Dec 2;28(12):2525-2526. doi: 10.1016/j.ymthe.2020.11.005. Epub 2020 Nov 10.
No abstract available

Publication types

  • Comment

MeSH terms

  • CRISPR-Cas Systems*
  • Congenital Bone Marrow Failure Syndromes
  • Hematopoietic Stem Cell Transplantation*
  • Mutation
  • Neutropenia / congenital

Supplementary concepts

  • Neutropenia, Severe Congenital, Autosomal Recessive 3