Getting Back to Normal: Correcting SCN by Universal or Precision Strikes
Mol Ther
.
2020 Dec 2;28(12):2525-2526.
doi: 10.1016/j.ymthe.2020.11.005.
Epub 2020 Nov 10.
Authors
Hrishikesh M Mehta
1
,
Seth J Corey
2
Affiliations
1
Department of Pediatrics and Cancer Biology, Cleveland Clinic, 9500 Euclid Avenue, Cleveland, OH 44195, USA.
2
Department of Pediatrics and Cancer Biology, Cleveland Clinic, 9500 Euclid Avenue, Cleveland, OH 44195, USA. Electronic address: coreylab@yahoo.com.
PMID:
33176167
PMCID:
PMC7704740
DOI:
10.1016/j.ymthe.2020.11.005
No abstract available
Publication types
Comment
MeSH terms
CRISPR-Cas Systems*
Congenital Bone Marrow Failure Syndromes
Hematopoietic Stem Cell Transplantation*
Mutation
Neutropenia / congenital
Supplementary concepts
Neutropenia, Severe Congenital, Autosomal Recessive 3