The Platform Vector Gene Therapies Project: Increasing the Efficiency of Adeno-Associated Virus Gene Therapy Clinical Trial Startup

Hum Gene Ther. 2020 Oct;31(19-20):1034-1042. doi: 10.1089/hum.2020.259.
No abstract available

Publication types

  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Clinical Trials as Topic / standards*
  • Dependovirus / genetics*
  • Genetic Therapy / methods*
  • Genetic Therapy / standards*
  • Genetic Vectors / administration & dosage*
  • Genetic Vectors / genetics
  • Humans
  • Rare Diseases / genetics
  • Rare Diseases / therapy*