Base editing rescues hearing in mice

Nat Rev Drug Discov. 2020 Jul;19(7):443. doi: 10.1038/d41573-020-00106-z.
No abstract available

Keywords: Biotechnology; Drug discovery; Gene therapy.

Publication types

  • Comment

MeSH terms

  • Animals
  • CRISPR-Cas Systems*
  • Disease Models, Animal
  • Gene Editing*
  • Mice