False Negative Carrier Screening in Spinal Muscular Atrophy

J Child Neurol. 2020 Mar;35(4):274-277. doi: 10.1177/0883073819891269. Epub 2019 Dec 20.

Abstract

We describe a case of spinal muscular atrophy diagnosed in an infant despite previous parental carrier testing suggesting low risk of the disease. This case report explains how this situation arose and illustrates that clinicians need to perform diagnostic testing in children where clinical suspicion for spinal muscular atrophy is high, regardless of the result of previous parental carrier testing, because of the risk of false negative results.

Keywords: SMA; carrier screening; false negative tests; spinal muscular atrophy.

Publication types

  • Case Reports

MeSH terms

  • False Negative Reactions
  • Female
  • Genetic Testing / methods*
  • Humans
  • Infant
  • Muscular Atrophy, Spinal / diagnosis*
  • Muscular Atrophy, Spinal / drug therapy
  • Muscular Atrophy, Spinal / genetics*
  • Oligonucleotides / therapeutic use
  • Survival of Motor Neuron 1 Protein / genetics*

Substances

  • Oligonucleotides
  • SMN1 protein, human
  • Survival of Motor Neuron 1 Protein
  • nusinersen