Zmax test for delayed effect in immuno-oncology clinical trials

J Biopharm Stat. 2020 Mar;30(2):244-266. doi: 10.1080/10543406.2019.1632873. Epub 2019 Jul 10.

Abstract

Delayed separation in survival curves has been observed in immuno-oncology clinical trials. Under this situation, the classic log-rank test may confront high power loss. In this paper, we consider a Zmax test, which is the maximum of the log-rank test and a Fleming-Harrington test. Simulation studies indicate that the Zmax test not only controls the Type I error rate but also maintains good power under different delayed effect models. The asymptotic properties of the Zmax test are also established, which further supports its robustness. We apply the Zmax test to two data sets reported in recent immuno-oncology clinical trials, in which Zmax has exhibited remarkable improvement over the conventional log-rank test.

Keywords: Fleming-Harrington; Zmax test; clinical trials; delayed effect; immuno-oncology; log-rank test; weighted log-rank test.

Publication types

  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Antineoplastic Agents, Immunological / immunology
  • Antineoplastic Agents, Immunological / therapeutic use*
  • Clinical Trials as Topic / methods
  • Clinical Trials as Topic / statistics & numerical data*
  • Humans
  • Medical Oncology / methods
  • Medical Oncology / statistics & numerical data*
  • Neoplasms / drug therapy*
  • Neoplasms / epidemiology
  • Neoplasms / immunology
  • Survival Rate / trends
  • Treatment Outcome

Substances

  • Antineoplastic Agents, Immunological