[The time has come of a therapeutic (re)positioning of the ultra-rare diseases]

Med Sci (Paris). 2018 Dec;34(12):1019-1021. doi: 10.1051/medsci/2018302. Epub 2019 Jan 9.

[Article in French]

Authors

Cécile Martinat¹, Marc Peschanski²

Affiliations

¹ Unité mixte de recherche Inserm 861/UEVE I-Stem, 28, rue Henri Desbruères 91100 Corbeil-Essonnes, France.
² CECS/AFM, I-Stem, 28, rue Henri Desbruères 91100 Corbeil-Essonnes, France.

PMID: 30623755
DOI: 10.1051/medsci/2018302

No abstract available

Publication types

Editorial

MeSH terms

Cell- and Tissue-Based Therapy / economics
Cell- and Tissue-Based Therapy / methods
Cell- and Tissue-Based Therapy / trends
Drug Discovery / economics
Drug Discovery / trends
Drug Repositioning* / economics
Drug Repositioning* / methods
Drug Repositioning* / trends
Genetic Predisposition to Disease
Genetic Therapy / economics
Genetic Therapy / methods
Genetic Therapy / trends
Humans
Induced Pluripotent Stem Cells / physiology
Prevalence
Rare Diseases / economics
Rare Diseases / epidemiology
Rare Diseases / genetics
Rare Diseases / therapy*
Therapies, Investigational / economics
Therapies, Investigational / methods
Therapies, Investigational / trends