Small Interfering RNA-Mediated Control of Virus Replication in the CNS Is Therapeutic and Enables Natural Immunity to West Nile Virus

Cell Host Microbe. 2018 Apr 11;23(4):549-556.e3. doi: 10.1016/j.chom.2018.03.001. Epub 2018 Mar 29.

Abstract

No vaccines or therapeutics are licensed for West Nile virus (WNV), a mosquito-transmitted neuroencephalitic flavivirus. The small interfering RNA siFvEJW targets a conserved sequence within the WNV E protein and limits virus infection. Using a rabies virus-derived neuron-targeting peptide (RVG9R) and an intranasal route for delivering siFvEJW to the CNS, we demonstrate that treatment of WNV-infected mice at late stages of neuroinvasive disease results in recovery. Selectively targeting virus in the CNS lowers viral burdens in the brain, reduces neuropathology, and results in a 90% survival rate at 5-6 days post-infection (when viral titers peak in the CNS), while placebo-treated mice succumb by days 9-10. Importantly, CNS virus clearance is achieved by humoral and cell-mediated immune responses to WNV infection in peripheral tissues, which also engender sterilizing immunity against subsequent WNV infection. These results indicate that intranasal RVG9R-siRNA treatment offers efficient late-stage therapy and facilitates natural long-term immunity against neuroinvasive flaviviruses.

Keywords: CNS delivery; West Nile virus; flavivirus; intranasal treatment; natural immunity; rabies virus glycoprotein; siRNA; therapeutics.

MeSH terms

  • Animals
  • Brain / immunology
  • Brain / virology*
  • Disease Models, Animal
  • Drug Carriers*
  • Mice
  • Placebos / administration & dosage
  • RNA, Small Interfering / metabolism*
  • Rabies virus / genetics*
  • Survival Analysis
  • Virus Replication / drug effects*
  • West Nile Fever / immunology
  • West Nile Fever / prevention & control*
  • West Nile virus / immunology
  • West Nile virus / physiology*

Substances

  • Drug Carriers
  • Placebos
  • RNA, Small Interfering