Gene Therapy for Cerebral Adrenoleukodystrophy

N Engl J Med. 2018 Feb 1;378(5):490-491. doi: 10.1056/NEJMc1715427.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Adrenoleukodystrophy*
  • Hematopoietic Stem Cell Transplantation*
  • Humans