Gene Therapy for Cerebral Adrenoleukodystrophy
N Engl J Med
.
2018 Feb 1;378(5):490-491.
doi: 10.1056/NEJMc1715427.
Authors
David A Williams
1
,
Florian Eichler
2
,
Christine Duncan
3
Affiliations
1
Boston Children’s Hospital, Boston, MA dawilliams@childrens.harvard.edu
2
Massachusetts General Hospital, Boston, MA
3
Dana–Farber Cancer Institute, Boston, MA
PMID:
29385368
DOI:
10.1056/NEJMc1715427
No abstract available
Publication types
Letter
Comment
MeSH terms
Adrenoleukodystrophy*
Hematopoietic Stem Cell Transplantation*
Humans