[Intrathecal Nursinersen Therapy in Children with Spinal Muscular Atrophy and Spinal Deformities]

Klin Padiatr. 2018 Jul;230(4):231-233. doi: 10.1055/s-0044-100621. Epub 2018 Jan 29.
[Article in German]
No abstract available

MeSH terms

  • Child
  • Humans
  • Injections, Spinal / adverse effects
  • Muscular Atrophy, Spinal / drug therapy*
  • Neuromuscular Agents / administration & dosage*
  • Oligonucleotides / administration & dosage*
  • Spinal Puncture / adverse effects
  • Spine / abnormalities*

Substances

  • Neuromuscular Agents
  • Oligonucleotides
  • nusinersen