No abstract available
MeSH terms
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Anemia, Sickle Cell / genetics
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Anemia, Sickle Cell / therapy*
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CRISPR-Cas Systems
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Carrier Proteins / genetics*
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Gene Editing / methods*
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Genetic Therapy / methods
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Humans
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Mutation
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Nuclear Proteins / genetics*
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Repressor Proteins
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Zinc Finger Nucleases / metabolism
Substances
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BCL11A protein, human
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Carrier Proteins
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Nuclear Proteins
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Repressor Proteins
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Zinc Finger Nucleases