Targeting Therapeutic Oligonucleotides

N Engl J Med. 2017 Jan 5;376(1):86-88. doi: 10.1056/NEJMcibr1613559.
No abstract available

MeSH terms

  • Base Pairing
  • Drug Design
  • Hepatocytes / metabolism
  • Humans
  • Oligonucleotides, Antisense / administration & dosage*
  • Oligonucleotides, Antisense / metabolism
  • RNA, Small Interfering / administration & dosage*
  • RNA, Small Interfering / metabolism
  • RNAi Therapeutics

Substances

  • Oligonucleotides, Antisense
  • RNA, Small Interfering