Personalized models reveal mechanistic and therapeutic insights into CEP290-associated Leber congenital amaurosis

Stem Cell Investig. 2016 Oct 25:3:65. doi: 10.21037/sci.2016.10.03. eCollection 2016.

Authors

Devin S McDougald¹, Eric Kmiec², Jason A Mills¹

Affiliations

¹ Center for Advanced Retinal and Ocular Therapeutics, F.M. Kirby Center for Molecular Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104, USA.
² Gene Editing Institute, Center for Translational Cancer Research, Helen F. Graham Cancer Center & Research Institute, Christiana Care Health System, Newark, DE 19702, USA.

No abstract available

Publication types

Editorial
Comment