Challenges ahead for trials in Friedreich's ataxia

Lancet Neurol. 2016 Dec;15(13):1300-1301. doi: 10.1016/S1474-4422(16)30281-2.

Authors

David R Lynch¹, Elizabeth Kichula²

Affiliations

¹ Departments of Pediatrics and Neurology, Children's Hospital of Philadelphia, Philadelphia, PA 19104-4318, USA; Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. Electronic address: lynchd@mail.med.upenn.edu.
² Departments of Pediatrics and Neurology, Children's Hospital of Philadelphia, Philadelphia, PA 19104-4318, USA.

PMID: 27839636
DOI: 10.1016/S1474-4422(16)30281-2

No abstract available

Publication types

Comment

MeSH terms

Friedreich Ataxia / genetics*
Humans
Phenotype
Trinucleotide Repeats*