Reduction of Factor VIII Inhibitor Titers During Immune Tolerance Induction With Recombinant Factor VIII-Fc Fusion Protein

Pediatr Blood Cancer. 2016 May;63(5):922-4. doi: 10.1002/pbc.25874. Epub 2016 Jan 6.

Abstract

The development of inhibitors toward factor VIII (FVIII) is a common and serious complication of hemophilia A (HA) therapy. Patients with hemophilia who develop inhibitors often undergo time- and resource-intensive immune tolerance induction (ITI) protocols. We report a 15-month-old male with severe HA and a high-titer inhibitor that occurred while receiving prophylactic treatment with recombinant FVIII (rFVIII), in whom significant inhibitor titer reduction was achieved with thrice weekly infusions of a new, prolonged half-life rFVIII-Fc fusion protein product (trade name Eloctate). Further studies are warranted to explore the potential of Eloctate in ITI protocols.

Keywords: eloctate; factor VIII inhibitors; hemophilia A; immune tolerance induction; recombinant factor VIII-Fc fusion protein.

Publication types

  • Case Reports

MeSH terms

  • Blood Coagulation Factor Inhibitors / immunology*
  • Desensitization, Immunologic*
  • Factor VIII* / administration & dosage
  • Factor VIII* / antagonists & inhibitors
  • Factor VIII* / genetics
  • Factor VIII* / immunology
  • Hemophilia A / drug therapy*
  • Hemophilia A / immunology
  • Humans
  • Immune Tolerance / drug effects*
  • Infant
  • Male
  • Receptors, Fc* / administration & dosage
  • Receptors, Fc* / genetics
  • Receptors, Fc* / immunology
  • Recombinant Fusion Proteins / administration & dosage
  • Recombinant Fusion Proteins / genetics
  • Recombinant Fusion Proteins / immunology

Substances

  • Blood Coagulation Factor Inhibitors
  • Receptors, Fc
  • Recombinant Fusion Proteins
  • F8 protein, human
  • Factor VIII