Challenges of clinical trial design for DMD
Neuromuscul Disord
.
2015 Dec;25(12):932-5.
doi: 10.1016/j.nmd.2015.10.007.
Epub 2015 Oct 23.
Authors
Valeria Ricotti
1
,
Francesco Muntoni
2
,
Thomas Voit
3
Affiliations
1
Dubowitz Neuromuscular Centre, UCL Institute of Child Health and Great Ormond Street Hospital, London, UK. Electronic address: v.ricotti@ucl.ac.uk.
2
Dubowitz Neuromuscular Centre, UCL Institute of Child Health and Great Ormond Street Hospital, London, UK.
3
NIHR Biomedical Research Centre, UCL Institute of Child Health and Great Ormond Street Hospital, London, UK.
PMID:
26584589
DOI:
10.1016/j.nmd.2015.10.007
No abstract available
MeSH terms
Animals
Clinical Trials as Topic*
Humans
Male
Muscular Dystrophy, Duchenne / drug therapy*
Phenotype