Cystic fibrosis transmembrane conductance regulator biomarkers in 'real life': can we evaluate individual efficacy of cystic fibrosis transmembrane conductance regulator therapy?

Ther Adv Respir Dis. 2015 Aug;9(4):198-200. doi: 10.1177/1753465815579364.
No abstract available

Publication types

  • Letter

MeSH terms

  • Adolescent
  • Adult
  • Aminophenols / pharmacology
  • Aminophenols / therapeutic use*
  • Biomarkers / metabolism
  • Child
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis / physiopathology
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Cystic Fibrosis Transmembrane Conductance Regulator / metabolism*
  • Female
  • Humans
  • Male
  • Mutation
  • Quinolones / pharmacology
  • Quinolones / therapeutic use*
  • Treatment Outcome
  • Young Adult

Substances

  • Aminophenols
  • Biomarkers
  • Quinolones
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor