209th ENMC International Workshop: Outcome Measures and Clinical Trial Readiness in Spinal Muscular Atrophy 7-9 November 2014, Heemskerk, The Netherlands

Neuromuscul Disord. 2015 Jul;25(7):593-602. doi: 10.1016/j.nmd.2015.04.009. Epub 2015 Apr 28.

Authors

Richard Finkel¹, Enrico Bertini², Francesco Muntoni³, Eugenio Mercuri⁴; ENMC SMA Workshop Study Group

Collaborators

Affiliations

¹ Nemours Children's Hospital, Orlando, USA. Electronic address: rfinkel@nemours.org.
² UCL Institute of Child Health, Dubowitz Neuromuscular Centre, London, UK.
³ Bambino Gesu Children's Research Hospital, Rome, Italy.
⁴ Pediatric Neurology Unit, Catholic University, Rome, Italy.

PMID: 26045156
DOI: 10.1016/j.nmd.2015.04.009

No abstract available

Publication types

Congress
Research Support, Non-U.S. Gov't

MeSH terms

Animals
Biomarkers / metabolism
Clinical Trials as Topic*
Disease Models, Animal
Humans
Muscular Atrophy, Spinal / classification
Muscular Atrophy, Spinal / diagnosis*
Muscular Atrophy, Spinal / genetics
Muscular Atrophy, Spinal / therapy*
Netherlands
Outcome Assessment, Health Care*

Substances

Biomarkers