Suppression of choroidal neovascularization through inhibition of APE1/Ref-1 redox activity

Invest Ophthalmol Vis Sci. 2014 Jun 26;55(7):4461-9. doi: 10.1167/iovs.14-14451.

Abstract

Purpose: The redox function of APE1/Ref-1 is a key regulator in pathological angiogenesis, such as retinal neovascularization and tumor growth. In this study, we examined whether inhibition of APE1/Ref-1 redox function by a small molecule inhibitor E3330 suppresses experimental choroidal neovascularization (CNV) in vitro and in vivo.

Methods: Primate choroid endothelial cells (CECs) received treatment of 0 to 100 μM E3330 alone or cotreatment of E3330 and 500 μg/mL anti-VEGF antibody bevacizumab. Choroid endothelial cell angiogenic function was examined by cell proliferation, migration, and tube formation assays. The effects of E3330 on NF-κB and STAT3 signaling pathways were determined by reporter gene assay, Western blot, and ELISA. Laser-induced CNV mouse model was used to test the effects of E3330 in vivo. Potential toxicity of E3330 was evaluated by TUNEL assay.

Results: The E3330 of 25 to 100 μM dose-dependently suppressed CEC proliferation, migration, and tube formation, in the absence of noticeable cell toxicity. Lower doses of E3330 (10-20 μM) reduced the transcriptional activity of NF-κB and STAT3 without affecting protein phosphorylation of both molecules. At the same time, E3330 downregulated MCP-1 production in CECs. The antiangiogenic effect of E3330 was comparable and additive to bevacizumab. The E3330 effectively attenuated the progression of laser-induced CNV in mice after a single intravitreal injection.

Conclusions: The APE1/Ref-1 redox function regulates multiple transcription factors and inflammatory molecules, and is essential for CEC angiogenesis. Specific inhibition of APE1/Ref-1 redox function with E3330 may represent a promising novel treatment for wet AMD.

Keywords: APE1/Ref-1; antiangiogenesis; choroidal neovascularization; redox function; transcription factors.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antibodies, Monoclonal, Humanized / pharmacology
  • Benzoquinones / pharmacology*
  • Bevacizumab
  • Blotting, Western
  • Cell Line
  • Cell Movement / drug effects
  • Cell Proliferation / drug effects
  • Chemokine CCL2 / metabolism
  • Choroid / blood supply
  • Choroidal Neovascularization / pathology
  • Choroidal Neovascularization / prevention & control*
  • DNA-(Apurinic or Apyrimidinic Site) Lyase / antagonists & inhibitors*
  • Disease Models, Animal*
  • Dose-Response Relationship, Drug
  • Endothelial Cells / drug effects
  • Endothelial Cells / metabolism
  • Endothelial Cells / pathology
  • Enzyme-Linked Immunosorbent Assay
  • Humans
  • In Situ Nick-End Labeling
  • Intravitreal Injections
  • Macaca mulatta
  • Male
  • Mice
  • Mice, Inbred C57BL
  • NF-kappa B / metabolism
  • Propionates / pharmacology*
  • STAT3 Transcription Factor / metabolism

Substances

  • Antibodies, Monoclonal, Humanized
  • Benzoquinones
  • Chemokine CCL2
  • NF-kappa B
  • Propionates
  • STAT3 Transcription Factor
  • Stat3 protein, mouse
  • E 3330
  • Bevacizumab
  • Apex1 protein, mouse
  • DNA-(Apurinic or Apyrimidinic Site) Lyase