Targeting protein-protein interactions to rescue Δf508-cftr: a novel corrector approach to treat cystic fibrosis

EMBO Mol Med. 2013 Oct;5(10):1462-4. doi: 10.1002/emmm.201303301. Epub 2013 Aug 27.
No abstract available

Keywords: drug discovery; ion channel; lung disease; proteostasis; therapy.

Publication types

  • Research Support, Non-U.S. Gov't
  • Comment

MeSH terms

  • Animals
  • Bronchi / cytology*
  • Cystic Fibrosis Transmembrane Conductance Regulator / metabolism*
  • Humans
  • Small Molecule Libraries / metabolism*

Substances

  • Small Molecule Libraries
  • cystic fibrosis transmembrane conductance regulator delta F508
  • Cystic Fibrosis Transmembrane Conductance Regulator