Eltrombopag fails to improve severe thrombocytopenia in late-stage dyskeratosis congenita and diamond-blackfan-anaemia

Thromb Haemost. 2012 Aug;108(2):397-8. doi: 10.1160/TH12-02-0121. Epub 2012 Jun 28.
No abstract available

Publication types

  • Case Reports
  • Letter

MeSH terms

  • Administration, Oral
  • Adolescent
  • Adult
  • Anemia, Diamond-Blackfan / drug therapy*
  • Anemia, Diamond-Blackfan / genetics
  • Benzoates / therapeutic use*
  • Cardiology / methods
  • Dyskeratosis Congenita / drug therapy*
  • Dyskeratosis Congenita / genetics
  • Female
  • Humans
  • Hydrazines / therapeutic use*
  • Male
  • Megakaryocytes / cytology
  • Pyrazoles / therapeutic use*
  • Receptors, Thrombopoietin / agonists
  • Thrombocytopenia / drug therapy*
  • Thrombocytopenia / etiology
  • Treatment Outcome

Substances

  • Benzoates
  • Hydrazines
  • Pyrazoles
  • Receptors, Thrombopoietin
  • eltrombopag