Polyethylene glycol-modified adenosine deaminase improved lung disease but not liver disease in partial adenosine deaminase deficiency

J Allergy Clin Immunol. 2009 Oct;124(4):848-50. doi: 10.1016/j.jaci.2009.07.003. Epub 2009 Aug 8.
No abstract available

Publication types

  • Case Reports
  • Letter
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenosine Deaminase / deficiency*
  • Adenosine Deaminase / therapeutic use
  • Erythrocytes / enzymology
  • Erythrocytes / metabolism
  • Follow-Up Studies
  • Humans
  • Immunoglobulins / blood
  • Infant, Newborn
  • Liver Diseases / complications
  • Liver Diseases / drug therapy*
  • Liver Diseases / enzymology
  • Lung Diseases / complications
  • Lung Diseases / drug therapy*
  • Lung Diseases / enzymology
  • Lymphocytes / enzymology
  • Lymphocytes / metabolism
  • Male
  • Severe Combined Immunodeficiency / complications
  • Severe Combined Immunodeficiency / drug therapy*
  • Severe Combined Immunodeficiency / enzymology

Substances

  • Immunoglobulins
  • Adenosine Deaminase
  • pegademase bovine