PTC124 for cystic fibrosis

Lancet. 2009 Apr 25;373(9673):1426; author reply 1426-7. doi: 10.1016/S0140-6736(09)60819-9.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Codon, Nonsense / drug effects*
  • Codon, Terminator / drug effects*
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics
  • Genetic Therapy / adverse effects
  • Humans
  • Oxadiazoles / adverse effects
  • Oxadiazoles / pharmacology*
  • Retroelements / drug effects*

Substances

  • Codon, Nonsense
  • Codon, Terminator
  • Oxadiazoles
  • Retroelements
  • ataluren