[Molecular pathogenesis and therapeutic targets of lysosomal diseases]

Seikagaku. 2007 Jul;79(7):678-82.
[Article in Japanese]
No abstract available

Publication types

  • Review

MeSH terms

  • 1-Deoxynojirimycin / analogs & derivatives
  • 1-Deoxynojirimycin / therapeutic use
  • Animals
  • Anti-Inflammatory Agents, Non-Steroidal / therapeutic use
  • Aspirin / therapeutic use
  • Bone Marrow Transplantation
  • Disease Models, Animal
  • G(M2) Activator Protein / genetics
  • Genetic Therapy
  • Humans
  • Lysosomal Storage Diseases, Nervous System / genetics*
  • Lysosomal Storage Diseases, Nervous System / therapy*
  • Mutation
  • beta-N-Acetylhexosaminidases / genetics

Substances

  • Anti-Inflammatory Agents, Non-Steroidal
  • G(M2) Activator Protein
  • 1-Deoxynojirimycin
  • miglustat
  • beta-N-Acetylhexosaminidases
  • Aspirin