Neuroimage findings in 2-methyl-3-hydroxybutyryl-CoA dehydrogenase deficiency

Pediatr Neurol. 2007 Apr;36(4):264-7. doi: 10.1016/j.pediatrneurol.2006.11.014.

Abstract

A case of 2-methyl-3-hydroxybutyryl-coenzyme A dehydrogenase deficiency, an X-linked defect of isoleucine degradation, is reported. A 10-month-old male infant with developmental regression, visual impairment, movement disorder, and seizures, he suffered acute deterioration with multiorganic failure after a respiratory infection. Laboratory studies revealed hyperlactacidemia and increased excretion of 2-methyl-3-hydroxybutyric acid (2M3HBA) and tiglylglycine (TG). The diagnosis was established by molecular genetic analysis of the involved X-chromosome gene HADH2. The patient was hemizygous for the mutation R130C (c. 388C>T). Magnetic resonance imaging disclosed frontotemporal atrophy and bilateral signal abnormalities in the putamina. The presence of basal ganglia abnormalities and lactic acidemia, also shared by mitochondrial disorders, suggests a common pathophysiologic mechanism of damage.

Publication types

  • Case Reports

MeSH terms

  • 3-Hydroxyacyl CoA Dehydrogenases
  • Alcohol Oxidoreductases / deficiency*
  • Alcohol Oxidoreductases / genetics
  • Atrophy
  • Brain / metabolism
  • Brain / pathology*
  • Brain Diseases, Metabolic, Inborn / genetics
  • Brain Diseases, Metabolic, Inborn / metabolism*
  • Brain Diseases, Metabolic, Inborn / pathology*
  • Chromosomes, Human, X
  • Frontal Lobe / metabolism
  • Frontal Lobe / pathology
  • Humans
  • Infant
  • Isoleucine / metabolism
  • Magnetic Resonance Imaging*
  • Male
  • Putamen / metabolism
  • Putamen / pathology
  • Temporal Lobe / metabolism
  • Temporal Lobe / pathology

Substances

  • Isoleucine
  • Alcohol Oxidoreductases
  • 3-Hydroxyacyl CoA Dehydrogenases
  • 2-methyl-3-hydroxybutyryl-coenzyme A dehydrogenase