Molecular basis of the targeting of topoisomerase II-mediated DNA cleavage by VP16 derivatives conjugated to triplex-forming oligonucleotides

Nucleic Acids Res. 2006 Apr 5;34(6):1900-11. doi: 10.1093/nar/gkl126. Print 2006.

Abstract

Human topoisomerase II (topo II) is the cellular target for a number of widely used antitumor agents, such as etoposide (VP16). These agents 'poison' the enzyme and induce it to generate DNA breaks that are lethal to the cell. Topo II-targeted drugs show a limited sequence preference, triggering double-stranded breaks throughout the genome. Circumstantial evidence strongly suggests that some of these breaks induce chromosomal translocations that lead to specific types of leukaemia (called treatment-related or secondary leukaemia). Therefore, efforts are ongoing to decrease these secondary effects. An interesting option is to increase the sequence-specificity of topo II-targeted drugs by attaching them to triplex-forming oligonucleotides (TFO) that bind to DNA in a highly sequence-specific manner. Here five derivatives of VP16 were attached to TFOs. The active topo II poisons, once linked, induced cleavage 13-14 bp from the triplex end where the drug was attached. The use of triple-helical DNA structures offers an efficient strategy for targeting topo II-mediated cleavage to DNA specific sequences. Finally, drug-TFO conjugates are useful tools to investigate the mechanistic details of topo II poisoning.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antineoplastic Agents, Phytogenic / chemistry*
  • Antineoplastic Agents, Phytogenic / toxicity
  • DNA / chemistry*
  • DNA Damage
  • DNA Footprinting
  • DNA Topoisomerases, Type II / metabolism
  • Drug Delivery Systems
  • Enzyme Inhibitors / chemistry
  • Enzyme Inhibitors / toxicity
  • Etoposide / analogs & derivatives*
  • Etoposide / toxicity
  • Humans
  • Oligodeoxyribonucleotides / chemistry
  • Topoisomerase II Inhibitors*

Substances

  • Antineoplastic Agents, Phytogenic
  • Enzyme Inhibitors
  • Oligodeoxyribonucleotides
  • Topoisomerase II Inhibitors
  • triplex DNA
  • Etoposide
  • DNA
  • DNA Topoisomerases, Type II