No abstract available
MeSH terms
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Cystic Fibrosis / therapy*
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Cystic Fibrosis Transmembrane Conductance Regulator / genetics
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Exons
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Genetic Therapy*
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Humans
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Introns
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Models, Genetic
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Mutation
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RNA Splicing
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RNA, Messenger / genetics*
Substances
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CFTR protein, human
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RNA, Messenger
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Cystic Fibrosis Transmembrane Conductance Regulator