Antisense treatment directed against mutated Ki-ras in human colorectal adenocarcinoma

Gut. 2001 Feb;48(2):230-7. doi: 10.1136/gut.48.2.230.

Abstract

Background: Kirsten ras (Ki-ras) mutations are common in gastrointestinal cancer and one codon 12 mutation, glycine to valine, is particularly aggressive in colorectal cancer.

Aims: To investigate if this valine point mutation could be targeted with antisense oligonucleotides and to determine the efficacy of any antisense/mRNA interaction.

Methods: Twenty nine antisense oligonucleotides were screened against target and control Ki-ras RNA in a cell free system and against target and control cell lines in culture.

Results: The activity and specificity of the oligonucleotides varied. Results for the individual oligonucleotides were consistent in a cell free model and in cell culture using two different uptake promoters. Only one oligonucleotide was specific in its cleavage of target Ki-ras mRNA in the cell free system and appeared specific in cell culture, although changes in Ki-ras mRNA and protein expression following a single treatment could not be detected. Experiments in the cell free system showed that the point mutation is relatively inaccessible to oligonucleotides. Other sites on the Ki-ras RNA molecule, away from the point mutation, can be targeted more effectively.

Conclusions: Successful targeting of the clinically relevant Ki-ras point mutation with antisense oligonucleotides is difficult because of RNA structure at the mutated site and is inefficient compared with other sites on the Ki-ras mRNA.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenocarcinoma / genetics
  • Adenocarcinoma / therapy*
  • Cell Survival
  • Cell-Free System
  • Colorectal Neoplasms / genetics
  • Colorectal Neoplasms / therapy*
  • Genes, ras / genetics*
  • Genetic Therapy / methods*
  • Humans
  • Oligonucleotides, Antisense / genetics
  • Oligonucleotides, Antisense / therapeutic use*
  • Point Mutation / genetics*
  • RNA, Messenger
  • Thionucleotides / genetics
  • Treatment Outcome
  • Tumor Cells, Cultured

Substances

  • Oligonucleotides, Antisense
  • RNA, Messenger
  • Thionucleotides